Autori: D'Amico A

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Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient Cohorts

Upper limb progression in Duchenne muscular dystrophy: Insights from a 36-month longitudinal study using the PUL 20

Loss of ambulation in SMA III at the time of disease-modifying treatments: an international study

Workshop report: Findings from the 2025 Italian SMAkers Educational Initiative on SMA management in Italy

Onasemnogene Abeparvovec in Type I Spinal Muscular Atrophy: 24-Month Follow-Up From the Italian Registry

Italian validation of the SMA independence scale-upper limb module

Longitudinal Assessment of 4-Year HFMSE Changes in SMA II and III Patients Treated With Nusinersen

Italian validation of the SMA independence scale-upper limb module

Myostatin Levels in SMA Following Disease-Modifying Treatments: A Multi-Center Study

Patients on treatment with risdiplam in Italy: challenges in the interpretation of the real-world data

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