Raggruppamento Secondario: Atrofia Muscolare Spinale (SMA)

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Data

Sequential treatment with nusinersen, Zolgensma® and risdiplam in a paediatric patient with spinal muscular atrophytype 1: a case report

Italian validation of the SMA independence scale-upper limb module

Motor and neurocognitive profiles of children with symptomatic spinal muscular atrophy type 1 with two copies of SMN2 before and after treatment: a longitudinal observational study

Predicted and measured resting energy expenditure in children with spinal muscular atrophy 2

Longitudinal Assessment of 4-Year HFMSE Changes in SMA II and III Patients Treated With Nusinersen

Bulbar function in children with spinal muscular atrophy type 1 treated with nusinersen

Italian validation of the SMA independence scale-upper limb module

Myostatin Levels in SMA Following Disease-Modifying Treatments: A Multi-Center Study

Serial casting for contractures in SMA: consensus derived guidelines for treatment

Patients on treatment with risdiplam in Italy: challenges in the interpretation of the real-world data

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